Regulating PCCA gene expression by modulation of pseudoexon splicing patterns to rescue enzyme activity in propionic acidemia https://www.biorxiv.org/content/10.1101/2023.07.05.547835v1?med=mas
Regulating PCCA gene expression by modulation of pseudoexon splicing patterns to rescue enzyme activity in propionic acidemia https://www.biorxiv.org/content/10.1101/2023.07.05.547835v1?med=mas