Next steps for the optimization of exon therapy for Duchenne muscular dystrophy
Galina Filonova & Annemieke Aartsma-Rus
EXPERT OPINION ON BIOLOGICAL THERAPY. 2023;23(2): 133–43. doi:10.1080/14712598.2023.216907
https://www.tandfonline.com/doi/epdf/10.1080/14712598.2023.2169070