CRISPRa-induced upregulation of human LAMA1 compensates for LAMA2-deficiency in Merosin-deficient congenital muscular dystrophy https://www.biorxiv.org/content/10.1101/2023.03.06.531347v1?med=mas
CRISPRa-induced upregulation of human LAMA1 compensates for LAMA2-deficiency in Merosin-deficient congenital muscular dystrophy https://www.biorxiv.org/content/10.1101/2023.03.06.531347v1?med=mas