Reduction of retinal ganglion cell death in mouse models of familial dysautonomia using AAV-mediated gene therapy and splicing modulators https://www.biorxiv.org/content/10.1101/2023.05.22.541535v1?med=mas
Reduction of retinal ganglion cell death in mouse models of familial dysautonomia using AAV-mediated gene therapy and splicing modulators https://www.biorxiv.org/content/10.1101/2023.05.22.541535v1?med=mas