"CSL’s Hemgenix costs $3.5mn per dose, which makes it the most expensive drug in the world. Skysona and Zynteglo, which are gene therapies targeting a rare childhood brain disease and an inherited blood disorder, developed by the Cambridge, Massachusetts-based biotech Bluebird Bio, are the second- and third-most expensive drugs on the market. They are priced at $3mn and $2.8mn per dose, respectively."
#GeneTherapy #DrugDiscovery #DrugDevelopment #haemophilia
#raredisease
https://www.ft.com/content/8173d816-1167-4773-bad5-f565fed3ffde
@cyrilpedia is there a manufacturing reason why this is so expensive? or is it priced that way mainly to recoup development costs?
@azzurite This is much more expensive than making a small molecule drug or a biological like a monoclonal antibody. But nothing to justify a price tag like this.
@cyrilpedia Thanks, I hate it :D
@cyrilpedia hemgenix? i fell into a cauldron of it when i was a baby.